Time
6:45 PM - 8:00 PM (EDT)
Name
Following the Path: Progress Toward Genetic Therapies
Description

How might CF be treated at the cellular and genetic levels? What are the challenges and possible solutions to developing genetic-based therapies? What would a therapy look like for me? If you are asking yourself these questions, then this session is for you! Experts in the field will provide an overview of these strategies with a deep dive discussion on the potential application of gene-corrected airway epithelial stem cells. Come away from this session with a better understanding of the key challenges and barriers that need to be addressed in order to develop genetic and cellular therapies. Gain more insight about the strategies to treat all mutations, the importance of delivering therapy to specific cells and tissues, and how each approach might affect you as a potential participant in future trials. As this session will cover complex topics, it will be helpful for attendees to have a basic understanding of CF biology.

Art Brace Kara Foshay Brigitte Gomperts John Sheridan
Session Format
Information