Date
Thursday, April 16, 2020
Name
Beyond Modulators: Genetic Therapies on the Horizon
Session Format
Information
Advanced: This session will cover complex topics, so it will be helpful to have a basic knowledge of CF biology.
Description
How can CF be treated at the genetic level? What’s the difference between gene editing, gene replacement, and mRNA therapy? When will these therapies become a reality? If you are asking yourself these questions, then this session is for you! Experts in the field will provide a comprehensive overview of the various methods and strategies to genetically treat CF. Come away from this session with a better understanding of the key challenges that need to be addressed to develop a genetic therapy for all people with CF. Gain more insight about the strategies to treat all mutations and the importance of delivering therapy to specific cells and tissues. Because this session will cover complex topics, it will be helpful to have a basic knowledge of CF biology.